Randomised clinical trials: advantages and limitations of using parallel-group design or cross-over designs in the field of methylphenidate for ADHD

Article type
Year
Authors
Krogh HB1, Storebø OJ1, Kielsholm ML1, Nielsen SS1, Simonsen E1, Gluud C2
1Psychiatric Research Unit, Denmark
2Copenhagen Trial Unit, Denmark
Abstract
Objectives: Methylphenidate is the most commonly used drug for attention-deficit hyperactivity disorder (ADHD) in children and adolescents. Several randomised clinical trials have assessed the effects of the drug using either parallel-group or cross-over designs. We investigate advantages and limitations of these two designs for the assessment of methylphenidate for ADHD in children and adolescents. Furthermore, we investigate the risks of carry-over effect when using the cross-over design.

Methods: The methods used followed the Cochrane Handbook. Data from randomised clinical trials were included. Authors of cross-over trials where only end-of-period data were available were contacted to obtain data from all intervention periods. Meta-analyses were conducted and the results were presented in forest plots, and Chi² and I² were applied as tests for statistical heterogeneity.

Results: A total of 147 (n = 7134) cross-over trials and 38 (n = 5111) parallel-group trials were included. Differences in intervention effects were tested by comparing parallel-group trials to the first-period of cross-over trials and by analysing the first-period of cross-over trials pooled with parallel-group trials and comparing them to end-of cross-over trials (Chi² = 3.67, df = 1; P = 0.06; I² = 72.8%; 75 trials). The risk of carry-over effect was tested by comparing first-period to the end-of-trial period in cross-over trials (Chi² = 2.47, df = 1; P = 0.12; I² = 59.6%; 4 trials). Parallel-group trials are closer to the real world scenario, and offer better evaluation of the benefits.

Conclusions: Based on the results, both parallel-group trials and cross-over trials are suitable for investigating methylphenidate for children and adolescents with ADHD. The choice of design is, however, important to consider as the parallel-group design offers clear and more realistic benefits. Furthermore, data from cross-over trials are more difficult to include in systematic reviews.